In research published in Developmental Medicine & Child Neurology, investigators have developed a brief, reliable, and valid ...

The Muscular Dystrophy Association (MDA) is proud to announce the recipients of the 2026 MDA Legacy Awards, recognizing excellence in scientific and clinical research and saluting outstanding ...

Shares of  Regenxbio rose Monday in premarket trading after the company said its treatment for Duchenne muscular dystrophy delivered positive trial results, strengthening the case for a speedier ...

Solid Biosciences (SLDB) stock rises as a Phase 1/2 trial for its lead asset SGT-003 in Duchenne muscular dystrophy reaches ...

PPMD extends its heartfelt thanks to all Race to End Duchenne runners, donors, and volunteers who made the 2026 Walt Disney World (R) Marathon Weekend a memorable and meaningful success. To learn more ...

Muscle tissue damage appears when muscular dystrophy is induced in a mouse model (middle). But when researchers block the function of two genes that drive unwanted mitochondrial pore formation (right) ...

Jefferies analysts forecast a $1 billion market opportunity for each of Sarepta’s siRNA programs for facioscapulohumeral ...

The Food and Drug Administration awarded priority review status for a drug intended to treat a childhood-onset form of muscular dystrophy, according to the Chicago Tribune. Northbrook, Ill.-based ...

Nila Morton, a graduate student at Howard University, was excited to be traveling back to South Carolina for Thanksgiving after almost a year of being away from home. Morton, 25, was born with a rare ...

Rhys Hoskins flew from California to Philadelphia four months after he debuted in the majors. He had a charity event to attend at an aquarium in New Jersey. It was December 2017 and Hoskins ...

Your muscles need continuous maintenance to stay strong and healthy. Duchenne muscular dystrophy (DMD) happens when there is a change in a person's genetic instructions that affects the production of ...